
A rare condition that causes rapid, uncontrollable weight gain can now be treated, according to a recent phase 3 clinical trial published in The New England Journal of Medicine.

New estimates of rates of sepsis during pediatric hospitalizations have been obtained by a multicenter team of investigators, using clinical data from electronic health records.

A first‑ever gene‑regulation therapy tested in early‑phase clinical trials co‑led by Northwestern University Feinberg School of Medicine and Ann & Robert H. Lurie Children’s Hospital of Chicago has proven safe in children with Dravet syndrome who have exhausted conventional treatment options, according to a study published in the New England Journal of Medicine.

Ten years after undergoing bariatric surgery as teens, over half of study participants demonstrated not only sustained weight loss, but also resolution of obesity-related conditions, such as type 2 diabetes, high blood pressure and high cholesterol.

The lab of Yongchao C. Ma, PhD, has discovered a fundamental biological mechanism that could lead to new treatments for neurological diseases, such as spinal muscular atrophy (SMA) and autism, as well as different cancers.

Ann & Robert H. Lurie Children’s Hospital of Chicago is the first in Illinois to receive designation as a NORD Rare Disease Center of Excellence, becoming one of 40 U.S. academic medical centers selected to be a part of the first-of-it-kind national network of U.S. medical institutions dedicated to diagnosing, treating, and researching all rare…

Transgender and nonbinary youth experienced sustained improvements in depression and anxiety over two years after starting treatment with gender-affirming hormones, according to a recent study.

A new drug has been shown to be highly effective against pediatrics infections caused by respiratory syncytial virus (RSV).

The laboratory of YouYang Zhao, PhD, developed a unique nanoparticle to deliver genome editing technology, including CRISPR/Cas9, to vascular endothelial cells.

Ann & Robert H. Lurie Children’s Hospital of Chicago has recruited an internationally recognized surgeon-scientist, Thomas H. Inge, MD, PhD, as the hospital’s next surgeon-in-chief.
