A first of its kind drug called vosoritide may increase bone growth in children with achondroplasia, the most common form of dwarfism, according to findings from a recent clinical trial.
New findings have revealed previously unknown information about the genetic basis for Armfield XLID syndrome, a rare intellectual disability linked to genetic defects in the X chromosome.
Biomarkers using mass cytometry can assess patient response to an emerging treatment for pediatric brain tumors, according to a recent multi-center study.
Lifestyle advice has been only somewhat effective in controlling or slowing the progression of nonalcoholic fatty liver disease in children, according to a recent study published in Gastroenterology.
A Northwestern Medicine scientist and collaborators have used an AI-enhanced precision medicine approach to combine multiple views of human brain development as they seek to provide a roadmap for what causes subtypes of autism spectrum disorder.
Matthew Davis, MD, a pediatrician and internist with a focus on family health and community impact, has been named chair of the Department of Pediatrics at Feinberg and Ann & Robert H. Lurie Children’s Hospital of Chicago.
A specific cell signaling protein may be used to enhance the sensitivity of medulloblastoma tumors to immunotherapy, potentially improving quality of life for patients with the malignant pediatric brain cancer.
Children with difficult medical issues are more likely to experience social challenges at home, demonstrating the need for additional support and resources for these children in clinical settings.
Children with COVID-19 experience severe illness less frequently than adults, but the disease can still be dangerous, according to a recent study.
A novel drug called luspatercept may reduce blood transfusion burden for patients with transfusion-dependent beta-thalassemia, an inherited blood disorder.