In new clinical trials, a gene therapy for a serious blood disorder called beta-thalassemia significantly improved outcomes among patients, without serious side effects.
A drug called dasatinib was found to be safe and effective for children with chronic myeloid leukemia, according to a study published in the Journal of Clinical Oncology.
For the first time, scientists have measured the stress levels of fathers of premature babies during the transition between the Neonatal Intensive Care Unit and home and discovered fathers are more stressed than mothers.
More than half of infants with infantile-onset spinal muscular atrophy who were treated with nusinersen gained motor milestones, according to a recent Northwestern Medicine trial.
A comprehensive genomic analysis of the most common kidney cancer in children – found genetic mutations involving two distinct processes, potentially providing new opportunities for future treatments.
In research published in Nature Medicine, Northwestern Medicine scientists have found a molecule that stops the growth of an aggressive pediatric brain tumor for which there is no current treatment.
Children with congenital heart disease have a higher risk of epilepsy through adulthood, according to a recent Northwestern Medicine study.
Standard guidelines are needed for prescribing opioids to children discharged after a sickle cell disease pain episode, according to a recent Northwestern Medicine study.
Northwestern University has been awarded a grant from the National Institutes of Health to help scientists across the country study how environmental factors influence health outcomes for children.